Top speakers:
Andrzej Rys, Director, Health Systems, Medical Products and Innovation, DG SANTE
European Commission
Kristina Larsson, Head of Orphan Drugs, EMA
Bernard J. Grimm, Director, Healthcare Biotechnology, Europabio
Delphine Roulland, Senior Manager Public Affairs, EUCOPE
Ulrika Vestin, Swedish Association of Local Authorities and Regions (SKL),
Prof Maurizio Scarpa, Coordinator, European Reference Network for Hereditary Metabolic Diseases (MetabERN)
Anne Pariser, MD, Director, Office of Rare Diseases Research, National Center for Advancing Translational Sciences (NCATS), National Institutes of Health
Dr Vinciane Pirard, Co-Chair of Rare Disease & OMP Joint Task Force EFPIA-Europabio & Senior Director Public Affairs, Sanofi
Mark Rothera, Chief Executive Officer, Orchard Therapeutics
Stuart Peltz, Chief Executive Officer, PTC Therapeutics
Bob Smith, Senior Vice President, Global Gene Therapy Business, Pfizer
Sander van Deventer, Chief Scientific Officer, UniQure
Frederic Chereau, Chief Executive Officer, LogicBio Therapeutics
Marcus Guardian, Chief Operating Officer, EUnetHTA
