Locana
Locana is creating a new class of gene therapies by targeting disease causing mRNA. The Locana platform includes a portfolio of systems for modifying mRNA through delivery by gene therapy. These systems can modify dysfunctional mRNA associated with a range of genetic disorders, including neuromuscular, neurodegenerative and ocular diseases. Our unique approach creates a new class of gene therapies that is able to durably modify RNA across multiple mechanisms of action with the goal of making a meaningful difference in patients’ lives.
