
The World Orphan Drug Congress USA 2025 is the premier gathering for industry experts dedicated to advancing orphan drug development and rare disease therapies. This event brings together key stakeholders from biotech and pharma powerhouses, patient advocacy groups, regulatory agencies, investors, and beyond to drive innovation in the rare disease space.
The Mayo Clinic RNA Discovery and Translation Program brings together our renowned experts in discovery science, GMP manufacturing, computational biology, and investigator-initiated clinical trials. The program is designed to enable our researchers to fast-track emerging innovations in RNA based biomarkers and cures.